• FDA Approves Hemlibra to Treat for Hemophilia A Patients with Factor VIII Inhibitors
  • Normal in My World
  • New Version of Possible Gene Therapy for Hemophilia B, SPK-9001, Enrolling More Patients in Trial
  • First Hemophilia A Patient Enrolls in Phase 4 Trial for Eloctate Immune Tolerance Induction
  • Don’t Minimize Your Story!
  • Chris Bombardier Readies for Climb of Mount Vinson, Final of 7 Summits, with Help of Octapharma USA
  • Eloctate Improves Joint Health in Hemophilia A, Phase 3 Study Shows
  • FDA Accepts Bayer Application for BAY94-9027 to Possibly Treat Hemophilia A
  • Children’s National, NORD Partner to Create Rare Disease ‘Centers of Excellence’
  • Something New: Welcoming a Product to the Family
  • BioMarin’s Investigative Gene Therapy for Hemophilia A Wins FDA Breakthrough Designation
  • FDA Grants Orphan Drug Status to Gene Therapy Candidate SHP654 for Hemophilia A