uniQure Granted US Patent to Use FIX-Padua for Hemophilia B Gene Therapy
The U.S. Patent and Trademark Office has granted uniQure a third patent covering the formulation and use of the…
Articles by Alice Melão
Anticoagulant Protein TFPI Crucial to Bleeding Severity Profile of Hemophilia Patients, Study Says
A natural anticoagulant protein called tissue factor pathway inhibitor (TFPI) is critical for defining the bleeding severity profiles of…
High Rates of Undiagnosed Depression and Anxiety Found in Adults with Hemophilia, US Survey Says
Many hemophilia patients experience undiagnosed symptoms of depression and anxiety that can impact their ability to cope with the disease…
Mitsubishi Tanabe Launching Project to Develop Gene Therapies for Hemophilia B
Mitsubishi Tanabe Pharma is joining forces with researchers from Jichi Medical University to…
NHF, HFA Seek Additional Explanations From Bayer on Mislabeled Kogenate Recall
The National Hemophilia Foundation (NHF) and Hemophilia Federation of America (HFA) asked Bayer to clarify the risks to…
Interim Results of Alta Study Support SB-525’s Potential as Severe Hemophilia A Treatment
Investigational gene therapy SB-525 can safely induce durable clotting factor VIII (FVIII) activity in patients with severe hemophilia…
Questionnaires Offer Insight on Hemophilia Patients’ Quality of Life
Self-reported health outcomes of hemophilia patients provide useful and clinically valuable data on the efficacy of treatments, a population-based study…
Summit Fuels Discussion on New and Upcoming Hemophilia Treatments
For the second year, key pharmaceutical and academic leaders in hemophilia therapy development will gather at the Hemophilia Drug Development Summit…
Physical Activity Levels Low Among Hemophilia Patients in Japan , Study Finds
More than half of people with hemophilia in Japan fail to take part in sports or other physical activities at…
Two New Genetic Mutations Linked to Hemophilia A in Vietnamese Patients, Researchers Report
Two new mutations affecting the production of functional clotting factor VIII were identified in a group of Vietnamese patients with…