Single Dose of Gene Therapy AMT-061 Proves Effective in Hemophilia B
A single administration of AMT-061, an investigational gene therapy for people with severe and moderately severe hemophilia B, increased therapeutic…
Articles by Catarina Silva, MSc
First Hemophilia B Patient Treated with SB-FIX Gene Therapy in Phase 1/2 Trial
Sangamo Therapeutics has dosed the first patient in a Phase 1/2 clinical trial testing its investigational genome-editing therapy, SB-FIX, for…
Idelvion for Hemophilia B Now Available in Large 3500 IU Vial Size, CSL Behring Announces
Idelvion (albutrepenonacog alfa), a …
First Hemophilia B Patient Treated with AMT-061 in Phase 2b Trial
uniQure has treated the first patient in a Phase 2b dose-confirmation study of its investigational gene therapy, AMT-061, for…
Hemophilia Federation of America Gathering Memorabilia to Mark 25 Years of Service
The Hemophilia Federation of America (HFA) is seeking a variety of historical artifacts and records to add to its archival…
Companies Collaborating to Conduct Musical Workshop for Teens Affected by Bleeding Disorders
BioMarin Pharmaceutical Inc. is partnering with digital content agency Believe Limited to produce a three-day musical workshop for young members…
First Patient Enrolled in Phase 3 Trial of uniQure’s AMT-061 for Hemophilia B
UniQure has enrolled the first patient in its Phase 3 HOPE-B single-dose trial investigating the effectiveness and safety of AMT-061 in treating…
CVS Health Donates $260,000 To Bleeding Disorder Programs
In honor of Bleeding Disorder Awareness Month, celebrated in March, CVS Health is donating more than…
Oklahoma Medical Research Foundation, Shanghai RAAS Partner on Hemophilia Therapy
The Oklahoma Medical Research Foundation (OMRF) and Shanghai RAAS Blood Products are working together on the development of new…
Miniature Bleeding Model May Help Research into Wound Healing, Blood Disorders
Researchers at Emory University School of Medicine have developed a small-scale model system to study bleeding and clotting of wounds. The miniature…