The one-time gene therapy BBM-H901 (dalnacogene ponparvovec) has been officially approved in the Macao region of China for the treatment…
Articles by Margarida Maia, PhD
Many boys and young men with hemophilia regularly participate in sports. However, doing so frequently — particularly three or…
In boys and men with severe hemophilia A, starting prophylaxis — preventive treatment given regularly to reduce bleeding —…
Testing levels of thrombin — an enzyme that helps blood clot — in people with acquired hemophilia A could…
A single infusion of Hemgenix (etranacogene dezaparvovec-drlb) helped boost levels of factor IX (FIX), the clotting protein missing in…
Altuviiio (efanesoctocog alfa) reduced bleeding and was safe for boys and young men with severe hemophilia A, according to…
A new study highlights a hidden emotional burden for families living with hemophilia: the deep sense of guilt felt…
After five years of follow-up, Hemgenix (etranacogene dezaparvovec-drlb) was associated with durable factor IX (FIX) levels, lower bleeding rates,…
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Starting Hemlibra (emicizumab) early is safe and helps to prevent bleeding in babies with severe hemophilia A who…