Gene therapy for hemophilia B under review in US, Europe
Regulatory agencies in the U.S. and Europe are reviewing applications seeking the approval of fidanacogene elaparvovec, an experimental one-time…
Articles by Margarida Maia, PhD
$1.5M grant will fund research into TIPS to aid hemophilia A treatment
A researcher at the University at Buffalo has won a three-year grant worth $1.5 million to develop a way to…
Study finds care, treatment limited for hemophilia patients in Thailand
Hemophilia treatments in Thailand are limited due to a lack of budgetary resources, the high cost of medications, and…
Hemophilia A undertreated in female patients, carriers: US study
Female hemophilia AÂ patients and carriers have more frequent bleeding than males, yet a much smaller proportion receive…
Xoma closes $9.6M deal for rights to Ixinity for hemophilia B
Xoma closed a $9.6 million deal to buy from Aptevo Therapeutics the rights to receive a payment stream for…
Hemlibra Helps Keep Bleeding Under Control in Babies in HAVEN 7
Preventive treatment with Hemlibra (emicizumab) appears to be safe and helps keep bleeding under control in babies who have…
SerpinPC Found to Ease Bleeding in All Hemophilia Types for 1.5 Years
SerpinPC, a potential treatment for all types of hemophilia, from the drug development pipeline at Centessa Therapeutics, was…
Hemgenix Approved by FDA to Become 1st Gene Therapy for Hem B
The first gene therapy for adults with hemophilia B — branded as Hemgenix (etranacogene dezaparvovec) — has been approved by…
Enzyre Raises €12M to Advance At-home Blood-clotting Test for Hem A
Enzyre has raised €12 million (over $12 million) to speed the development of EnzyPad, a device that could…
Marstacimab Reduces Patients’ Bleeds, Even With Inhibitors
Treatment with marstacimab (PF-06741086), an experimental antibody-based therapy developed by Pfizer, reduced the number of bleeds in patients with…