People with hemophilia A who start on preventive treatment in the first years of life generally report better health-related…
Articles by Marisa Wexler, MS
Note: This story was updated May 8, 2023, to remove hemophilia as one of the specific indications the collaboration will…
Concizumab has been approved as a preventive treatment in Canada for hemophilia B patients ages 12 and older who…
Proteins from tardigrades — microscopic animals known for their ability to survive in extreme conditions — could be used to…
For children with severe hemophilia A who develop inhibitors — neutralizing antibodies that reduce the effectiveness of standard therapies…
The U.S. Food and Drug Administration (FDA) is extending its review of BioMarin Pharmaceutical’s request to approve the gene…
Most children with hemophilia A given Altuviiio (efanesoctocog alfa) once a week were bleed-free throughout about…
Most people with severe hemophilia A who were given once-weekly treatment with efanesoctocog alfa in the Phase 3…
The World Federation of Hemophilia (WFH) has launched a registry to monitor long-term outcomes of safety and effectiveness for people…
Treatment with the experimental gene therapy fidanacogene elaparvovec led to significant reductions in bleeding rates for men with moderately severe…