Genentech Opens HemeWork to Help Patients Realize Life Goals
Genentech has launched a program called HemeWork to support the professional development and career goals of people living with …
Articles by Forest Ray PhD
NHF Bleeding Disorder Education Programs Receive $500K CDC Grant
The National Hemophilia Foundation (NHF) has received a $500,000 grant from the Centers for Disease Control and Prevention…
RNA in Nanoparticles Leads to Efficient FVIII Production in Mice, Study Finds
Tiny particles containing RNA led to successful delivery and production of factor VIII (FVIII) — the clotting protein that…
Xperiome Platform Aims to Streamline Searches for Rare Diseases, Gain Patient Input
Raremark, an online rare disease patient community, has launched a digital platform called Xperiome, aimed at streamlining the…
Novo Nordisk Resumes Phase 3 Trials of Concizumab in Hemophilia A and B
Novo Nordisk has resumed its Phase 3 clinical trials investigating concizumab as a potential treatment for hemophilia A…
CDC Seeks Patients’ Input to Update Guidelines for Prescribing Opioids
The U.S. Centers for Disease Control and Prevention (CDC) is seeking input from people who live with pain, as…
Idelvion Helps Hemophilia B Patients Adhere to Prophylactic Treatment, Studies Show
Treatment with Idelvion (rIX-FP) helps children and adults with hemophilia B stick to prophylactic dosing schedules by reducing treatment…
FDA Clears CRYOcheck Lab Test of Factor VIII Activity in Hemophilia A
The U.S. Food and Drug Administration (FDA) has cleared for use CRYOcheck Chromogenic Factor VIII, Precision BioLogic‘s…
Enzyre Secures €1.4M to Advance Portable Device to Monitor Coagulation
Novalis Biotechnology is supporting a €1.4 million ($1.64 million) investment in Enzyre to finalize the development of a…
National Survey Seeks to Assess Full Social, Economic Burdens of Rare Diseases in US
The EveryLife Foundation for Rare Diseases has launched a nationwide National Burden of Rare Disease Survey to measure…