Tremeau and FDA Agree on Phase 3 Plan to Test Rofecoxib in Hemophilia Joint Pain
Tremeau Pharmaceuticals has received guidance from the U.S. Food and Drug Administration (FDA) on how to conduct a pivotal…
Articles by Magdalena Kegel
Gene Therapy Nearly Eliminates Hemophilia B Bleeding Episodes, Trial Shows
A hemophilia gene therapy developed by Spark Therapeutics and Pfizer nearly eliminated bleeding episodes in 10 patients who took part in…
Spark’s Gene Therapies to Treat Hemophilia A and B Advance in Clinical Trials
Three patients who received SPK-8011 — a gene therapy developed by Spark Therapeutics — for hemophilia A show increased production…
EU Grants €5.6 Million to Consortium Developing Sernova’s Cell Pouch Therapy for Hemophilia A Patients
The European Commission will award the Brussels-based HemAcure Consortium €5.6 million in next-stage funding of a therapy called Cell Pouch —  developed in…
CSL Behring’s Afstyla Allows Hemophilia A Patients to Use Less Factor Replacement, Analysis Shows
Hemophilia A patients treated with CSL Behring’s Afstyla (recombinant factor 8 single-chain) require less factor to control bleeding compared…
Aptevo’s Ixinity Found Safe, Effective in Kids Under 12 with Hemophilia B, Trial Shows
Ixinity (recombinant factor IX product, IB1001) was found to be safe and effective in previously treated children with hemophilia B…
Improvements in Gene Therapy Carriers Key Step in Hemophilia Treatment Development
Although gene therapy for hemophilia has reached clinical testing in humans, researchers continue to work toward improved delivery systems of…
Hemophilia B Hurts Education, Job Prospects for Both Adult Patients and Caregivers, Study Finds
Hemophilia B hurts educational and job prospects for both adults with the disease and caregivers of hemophiliac children, a recent…
Zepatier Found Effective, Safe Against Hepatitis C in Hemophilia Patients
Zepatier (elbasvir/grazoprevir) is an effective and safe treatment for hepatitis C infection in hemophilia patients and others with inherited blood disorders…
Distress Triggers Brain Changes in Hemophilia Children, Study Suggests
Psychological distress triggers microscopic changes in regions of hemophiliac children’s brains that deal with emotions and cognition — and the…