CSL Behring Donates Life-Saving Medicines to Developing Countries on World Hemophilia Day
CSL Behring marked World Hemophilia Day April 17 by shipping more than 10 million international units (IUs) of its medicines…
Articles by Margarida Azevedo, MSc
Hemlibra Named a Breakthrough Therapy for Hemophilia A Without Inhibitors
The U.S. Food and Drug Administration granted breakthrough therapy designation to Genentech’s Hemlibra (emicizumab-kxwh) for people with…
Deaths of 5 Hemophilia A Patients Not Related to Hemlibra Treatment, Genentech Says
The five adults with hemophilia A who died while using Hemlibra (emicizumab-kxwh) to treat their disease did not die of causes related…
BioMarin Wins Award for Getting Gene Therapy Facility Operational Ahead of Time
BioMarin Pharmaceutical has won an award for getting its new gene therapy facility in Novato, California, operational ahead of schedule.
Hemophilia B Patients Report Positive Experience with Ixinity Treatment, Aptevo Says
Patients with hemophilia B are reporting a mostly positive response to treatment with Ixinity (recombinant coagulation factor IX), according to new…
Sigilon Therapeutics’ Afibromer SIG-003 for Long-term Treatement of Hemophilia B Advances in EU
Sigilon Therapeutics’s Afibromer SIG-003 candidate for the long-term treatment of patients with…
Red Tie Campaign Aims to Protect Access to Affordable, Quality Care for People with Bleeding Disorders
The National Hemophilia Foundation (NHF) kicked off its 70th anniversary with an advocacy effort on Capitol Hill in Washington, D.C.
Free myPKFiT for Advate Now Available in the U.S.
myPKFiT for Advate, a free web-based software designed to personalize and assess preventive dosing regimens for some hemophilia A…
European Commission OKs Hemlibra to Preventively Treat Hemophilia A with Factor VIII Inhibitors
The European Commission has approved Hemlibra (emicizumab) for routine preventive treatment of bleeding episodes in people who have hemophilia…
AGC Biologics to Produce Hemophilia B Clotting Factor That Catalyst Is Testing in Clinical Trials
AGC Biologics has agreed to produce the hemophilia B clotting therapy that Catalyst Biosciences is testing in clinical trials, the…