A small survey study in Germany found that many people with severe hemophilia are not interested in receiving…
Articles by Marisa Wexler, MS
Children with hemophilia in areas with limited medical resources face a high risk of fatal brain bleeds, a danger…
The World Health Organization (WHO) executive board approved a resolution designed to improve access to diagnostic testing and treatment for…
Pfizer said the U.S. Food and Drug Administration (FDA) will review the company’s request to expand approval of its…
While nearly one-third of people living with hemophilia are female, a new global survey reveals that many of these…
BBM-H901 (dalnacogene ponparvovec), a gene therapy that’s approved in China for adults with moderate to severe hemophilia B, was…
Beqvez (fidanacogene elaparvovec-dzkt), a discontinued gene therapy for hemophilia B, was shown to help reduce joint bleeding in…
Geneventiv Therapeutics said it had a “positive and constructive” meeting with the U.S. Food and Drug Administration (FDA) on…
Biomarin Pharmaceutical is looking to sell off rights to Roctavian (valoctocogene roxaparvovec-rvox), its approved gene therapy for…
Hemophilia has a substantial impact on sexual function and well-being for many men with the disease, but they rarely…