A single infusion of the experimental gene therapy GS001 safely increased the levels of factor VIII (FVIII) — the missing…
Articles by Michela Luciano, PhD
A single infusion of Beqvez (fidanacogene elaparvovec-dzkt), a now-discontinued gene therapy for hemophilia B, led to sustained production…
An experimental therapy may help remove harmful antibodies that reduce the effectiveness of factor replacement therapies in hemophilia…
A young woman who sought emergency care for severe pain and swelling of her left hand five weeks after giving…
People living with hemophilia face a 46% higher risk of bone fractures than the general population, with that risk…
A new digital medical device, called florio HAEMO, may support more personalized care and help people with hemophilia better plan…
A structured rehabilitation program improved knee function, movement, and pain in people with hemophilia after total knee arthroplasty, a…
Note: This story was updated Jan. 20, 2026, to correct data on the number of boys on preventive FIX replacement…
People with hemophilia A and their caregivers, as well as healthcare providers, have shown a strong interest in a…
Hemlibra (emicizumab-kxwh) safely supports joint health in children with hemophilia A without inhibitors through three years of treatment,…