In a small study, children with hemophilia A had distinct changes in certain immune cells and inflammatory signaling molecules…
Articles by Michela Luciano, PhD
Nearly one-third of U.S. hemophilia treatment centers (HTCs) do not involve genetic counselors in patient care or refer patients…
Researchers spent years searching for a new treatment option for people with hemophilia A or B before arriving at the…
Children with severe hemophilia B who develop antibodies, also known as inhibitors, against coagulation factor IX (FIX) replacement therapies…
An experimental prenatal cell and gene therapy designed to restore production of the missing clotting protein in hemophilia A…
People with hemophilia, particularly those with more advanced joint disease, or hemophilic arthropathy, show altered walking patterns likely linked…
Many women carrying hemophilia-related mutations are not receiving the medical attention they need, according to a large-scale multinational study.
Roctavian (valoctocogene roxaparvovec-rvox) was associated with fewer bleeding episodes and less need for preventive treatment, or prophylaxis, in most…
Regular and sustained physical exercise — including aerobic activities, strength training, and balance exercises — may help ease chronic pain,…
A single dose of the gene therapy Roctavian (valoctocogene roxaparvovec-rvox) continues to prevent bleeds and the need for preventive…