A new combination of gene and cell-based therapy durably delivered therapeutic levels of factor VIII (FVIII) — the blood…
Articles by Steve Bryson, PhD
A new type of gene therapy that uses RNA instead of DNA led to rapid and prolonged…
Greater awareness of hemophilia and its symptoms is associated with better adherence to treatment by patients, and those…
Cells derived from hemophilia A patients — genetically reprogrammed to produce a functional…
A programmable mini-pump able to provide regular doses after surgery of FVIIa to hemophilia A patients with inhibitors —…
A lower dose of regular, preventive therapy with factor VIII concentrates was better at reducing bleeding events and improving joint…