News

November 18, 2020November 18, 2020

Enrollment Underway in Phase 4 Trial of Ixinity in Hemophilia B Patients Under Age 12

News

A Phase 4 trial investigating Ixinity as a prophylactic treatment for children under age 12 with hemophilia B has reached the halfway mark for its enrollment target, Medexus Pharmaceuticals announced. The international ... Read more

November 16, 2020November 16, 2020

DASH Diet Found to Yield Health Benefits in Adolescents With Hemophilia

News

The Dietary Approach to Stop Hypertension (DASH) diet yields beneficial health effects, reducing blood pressure, sugar, and fat, and increasing high-density lipoprotein (HDL) levels or so-called “good” cholesterol, in ... Read more

November 13, 2020November 13, 2020

Sanofi Genzyme Places Trials for Fitusiran on Hold

News

Due to the identification of new adverse events, Sanofi Genzyme has placed a dosing hold on its full clinical development program for fitusiran, an investigational treatment for hemophilia. The ... Read more

November 11, 2020November 11, 2020

Manual Therapy With Passive Stretching Helps Hemophilia Patients’ Joints, Study Finds

News

Manual therapy, in combination with passive stretching, can reduce the frequency of joint bleeds and improve joint health in people with hemophilia, a small study shows. The study, “The ... Read more

November 9, 2020November 9, 2020

Scientists Identify New Genetic Mutations Underlying Hemophilia A

News

Using a combination of genetic and functional approaches, scientists have identified new mutations in parts of the F8 gene that do not code for factor VIII (FVIII) in a ... Read more

November 6, 2020November 6, 2020

Hemlibra Safely Prevent Bleeds in Hemophilia A Patients Over Long Term, Trial Data Show

News

Hemlibra (emicizumab) continues to safely and effectively prevent bleedings in children and adults with hemophilia A, regardless of developing neutralizing inhibitors (antibodies) against synthetic factor VIII (FVIII), according to nearly ... Read more

November 5, 2020November 6, 2020

NORD Hosting ‘RareLaunch’ Workshops to Help Start Rare Disease Non-profits

News, syndicated

The National Organization for Rare Disorders (NORD)’s RareLaunch training program will host two days of free virtual workshops in December, with the aim of empowering leaders to start non-profit ... Read more

November 4, 2020November 4, 2020

Hemophilia Treatments Should Be Open to All, Regardless of Cost, ICER Told

News

The full range of hemophilia treatments should be made available to patients without consideration of cost or other barriers, leaders of patient associations and others argued at a public meeting hosted ... Read more

November 2, 2020November 2, 2020

Adynovate Prophylaxis Continues to Show Promise in Severe Hemophilia A, Trials’ Data Show

News

Prophylactic (preventive) treatment with Adynovate safely and effectively lowers the number of bleedings, including those in target joints, in children and adults with severe hemophilia A, according to data from two Phase ... Read more

October 30, 2020October 30, 2020

Acupuncture Might Work Better Than TENS to Reduce Chronic Joint Pain

News

Acupuncture was found to be more effective for reducing chronic joint pain in hemophilia patients than transcutaneous electrical nerve stimulation, or TENS, the results from a small clinical trial ... Read more