News

December 6, 2019December 6, 2019

HHS Secretary Alex Azar Touts White House Efforts to Cure Rare Diseases

News

Despite skyrocketing healthcare costs, President Trump is committed to protecting the 30 million or so Americans with rare diseases and ensuring timely, affordable access to lifesaving treatments, the nation’s ... Read more

December 6, 2019December 6, 2019

First 2 Adults with Severe Hemophilia A Respond Well to Gene Therapy in Clinical Trial

News

Bayer’s investigational gene therapy BAY 2599023 safely and effectively increased the levels of clotting factor VIII (FVIII) and prevented or lessened bleeding in the first two people with severe hemophilia A treated ... Read more

December 4, 2019December 4, 2019

Insurer Highmark Forges New Hemophilia Partnership Focused on Treatment, Management

News

As part of a new partnership focused on hemophilia treatment and management, members of insurer Highmark will receive medication exclusively from Option Care Health, Soleo Health, and the Hemophilia ... Read more

December 2, 2019December 2, 2019

Programmed Pump Infusions Aid in Care of Hemophilia A Patients After Surgery, Study Says

News

A programmable mini-pump able to provide regular doses after surgery of FVIIa to hemophilia A patients with inhibitors — those resistant to standard FVIII replacement therapy — successfully maintained expected levels ... Read more

November 27, 2019November 27, 2019

Lower-dose Preventive Therapy Reduced Bleeding Events in Thai Children with Hemophilia A, Study Shows

News

A lower dose of regular, preventive therapy with factor VIII concentrates was better at reducing bleeding events and improving joint function than on-demand treatment in children with hemophilia in ... Read more

November 25, 2019November 25, 2019

BioMarin Seeks Marketing Approval in Europe for its Investigational Gene Therapy, Valoctocogene Roxaparvovec

News

BioMarin Pharmaceuticals is seeking marketing approval in Europe for its investigational gene therapy, valoctocogene roxaparvovec, for the treatment of adults with severe hemophilia A. The company has submitted a ... Read more

November 22, 2019November 24, 2019

Pregnant Hemophilia B Carriers Have Three Times the Risk of Postpartum Hemorrhage, Swedish Study Finds

News

Pregnant women who are hemophilia B carriers have more than three times the risk of bleeding following childbirth than non-carriers, a register-based study done in Sweden has found. In ... Read more

November 20, 2019December 3, 2019

Insurer Highmark Partners With Soleo Health for Hemophilia Care, Management

News

Citing Soleo Health’s clinical expertise and data-reporting capabilities, U.S. national insurer Highmark has tapped the specialty pharmacy and infusion services provider to help care for its members who have ... Read more

November 18, 2019November 18, 2019

China Opens Blood Disease Platform, Collecting Patient Data to Improve Research and Treatment

News

The Analysis Group has partnered with China’s Institute of Hematology & Blood Diseases Hospital (IHBDH) to create the first blood disease research platform in that country. The new platform, called the ... Read more

November 15, 2019November 15, 2019

Proper Nutrition Lacking in Children with Hemophilia in Iraqi Province, Study Says

News

Proper nutrition is lacking in almost half of children with hemophilia in Iraq, with a significant portion of these children underweight compared to peers and a sizable number overweight, a study ... Read more

Pin It on Pinterest