Posing a Challenge: The True Cost of Mental Healthcare
Many years ago, while working in the association management world, I had a director who challenged his managers (including me) to calculate the “true” ... Read more
Updates
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Web-Based Calculator Helps Physicians to Finetune Dosage of Hemlibra for Hemophilia A Patients
BrightInsight has launched a web-based dosing calculator to help physicians select the correct loading and maintenance dose of the treatment Hemlibra according to the ... Read more -
What Job, the Man and the Legend, Has Taught Us About Suffering
It is no secret that I am a pastor in the United Methodist faith. Many times, I find that having children with bleeding disorders ... Read more -
This Graduation Season, Take Stock of Your Achievements
The month of May can be an emotional roller coaster for many. Social media fills up with parents bragging about their children’s latest accomplishments ... Read more -
Decision-making for Hemophilia Treatment Differs Between US and UK Doctors, Study Finds
U.S. doctors caring for people with hemophilia are more likely to make treatment decisions based on patient preferences than doctors in the U.K., who ... Read more
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Delving into the Depths of My DNA
I am a patient. I am an expert on my own health experiences. I ... -
Candidate Cell Therapy Controls Bleeding in Mouse Model of Hemophilia A
Sigilon Therapeutics’ candidate cell therapy for hemophilia A, called SIG-001, delivers sustained production of ... -
ASC Therapeutics Licenses Tech from Expression Therapeutics to Advance Gene Therapies
ASC Therapeutics has gotten exclusive rights to Expression Therapeutics‘ technology to develop liver-targeting hemophilia ... -
My Son Claims Victory Over His Mountain of Struggles
Our family took a recent trip to White Sands, New Mexico. The dunes were ... -
New Treatments Mean Summer Camps Can Focus on Fun
Summer is upon us. Our kids have big plans: sleeping in, watching television, playing ... -
Rare Diseases Constitute a ‘Public Health Issue,’ NCATS Director Warns
With 250 rare diseases newly identified every year, scientists can barely keep up — ...
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Europe’s CHMP Recommends Approval of Hemlibra to Treat Hemophilia A
News
Europe’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion supporting the approval of Hemlibra (emicizumab) for routine prophylaxis of bleeding episodes in hemophilia A patients with factor VIII inhibitors. Hemlibra is a humanized monoclonal antibody that ... Read more