An experimental prenatal cell and gene therapy designed to restore production of the missing clotting protein in hemophilia A showed maternal safety signs in a U.S. study in sheep. The therapy, called PLC-mcoET3, is designed to transplant genetically engineered cells into the fetus so they can produce factor VIII…
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I rarely participate in support groups on social media because some interactions leave me feeling more emotionally drained than supported. To be clear, there are genuinely kind and generous people in these communities. Many families have found lifesaving information, financial assistance, practical advice, and emotional solidarity through them. In…
Discussion
I spend a lot of time in the hospital, but not for the reasons most people think. As a hospice chaplain, I sit with patients who are nearing the end of life. It is a privilege to be with their families and friends as they prepare to say goodbye. The…
Discussion
I have medical records from my old hemophilia treatment center in Wisconsin dating back to the 1990s. Over the years, those old documents have turned out to be some of the most powerful tools in my healthcare journey. I was diagnosed in the ’90s with a rare…
Discussion
At the World Health Assembly (WHA), member states of the World Health Organization (WHO) unanimously adopted a resolution on Global Action to Advance Health Equity for People with Hemophilia and Other Bleeding Disorders to support better diagnosis, treatment, and fairer care for people with hemophilia and other bleeding…
Becoming educated and informed about hemophilia is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your hemophilia journey.
There is no cure for hemophilia yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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