The U.S. Food and Drug Administration (FDA) has given the go-ahead for Metagenomi Therapeutics to start a first-in-human clinical trial testing MGX-001, the company’s experimental gene-editing therapy for hemophilia A. The Phase 1/2 trial, dubbed INTEGR8, aims to test the safety and tolerability of MGX-001 and identify optimal…
Discussion
My son Caeleb faced some of the most challenging periods of his life at the same time the hemophilia treatment center (HTC) we used was looking for a replacement hematologist who specialized in bleeding disorders. He was 8 and had begun having target joint bleeds, and a high-titer…
Discussion
Somewhere along my journey as a “HemoWife,” I realized that being a good care partner and looking like one were two different jobs. One mattered to my marriage. The other seemed to exist largely for the benefit of an imaginary audience. We have a familiar image…
Discussion
Note: This story was updated Nov. 12, 2026, to clarify that the art, IV Couture, was created with unused supplies; used needles are a biohazard. G Shellye Horowitz, an artist and advocate who writes the column The Forgotten Factor for Hemophilia News Today, has been selected as a winner…
Discussion
Every Thanksgiving, my family gathers around a table crowded with turkey, stuffing, and more pie than anyone needs. We talk about football, the weather, and who drove the farthest. We almost never talk about health. That’s a missed opportunity. Since 2004, the U.S. surgeon general has recognized Thanksgiving as…
Becoming educated and informed about hemophilia is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes.
It helps to know others have been where you are now. Here’s a collection of our columnists’ words of wisdom to help you along on your hemophilia journey.
There is no cure for hemophilia yet, but here you can find more information about current therapeutic approaches, as well as experimental treatments that are in the pipeline.
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