Factor VII Treatment Approved by FDA for Hemophilia A and B with Inhibitors
The U.S. Food and Drug Administration (FDA) approved Sevenfact (coagulation factor VIIa [recombinant]-jncw) for the treatment and control of…
Articles by Joana Carvalho, PhD
Ixinity ‘Readily Available’ to Hemophilia B Patients Despite COVID-19 Pandemic, Medexus Says
Ixinity remains readily available to treat people with hemophilia B despite the current COVID-19 outbreak, Medexus…
Poor Joint Health Linked to Lower Self-Esteem in Adolescents with Hemophilia, Study Suggests
Poor joint health is associated with a higher risk of low self-esteem in adolescents with hemophilia, a study has…
Hemlibra Used to Prevent Bleeds Can Aid Joint Health in Hemophilia A, Trial Data Show
Prophylactic, or preventive, use of Hemlibra (emicizumab) promotes joint health in people with hemophilia A, according to a new…
AMT-061 Increases FIX Activity, Prevents Bleeds in Severe Hemophilia B Patients, Phase 2b Data Show
A single infusion of AMT-061 (etranacogene dezaparvovec), uniQure’s experimental gene therapy for the treatment of…
Top 10 Hemophilia Stories of 2019
Hemophilia News Today brought you daily coverage of important discoveries, treatment developments, clinical trials, and other key events related…
BioMarin Seeks Marketing Approval in Europe for its Investigational Gene Therapy, Valoctocogene Roxaparvovec
BioMarin Pharmaceuticals is seeking marketing approval in Europe for its investigational gene therapy, valoctocogene roxaparvovec, for the treatment of…
China Opens Blood Disease Platform, Collecting Patient Data to Improve Research and Treatment
The Analysis Group has partnered with China’s Institute of Hematology & Blood Diseases Hospital (IHBDH) to create the first blood disease…
Elimination of HCV in People with Bleeding Disorders Surpasses WHO Goals, Study Finds
Direct‐acting antiviral (DAA) therapy is especially effective at eliminating hepatitis C virus (HCV) in people with bleeding disorders,…
Novo Nordisk Partners with Bluebird Bio to Develop New Gene Therapies for Hemophilia, Other Disorders
Novo Nordisk has entered into a collaboration agreement with Bluebird Bio to develop new therapies based on…