Hemophilia A Treatment, Elocta, Eligible for Reimbursement in UK, Italy and France
Swedish Orphan Biovitrum AB recently announced that Eloctate (efmoroctocog alfa; brand name Elocta in Europe), a treatment for…
Articles by Margarida Azevedo, MSc
Sangamo’s Genome Editing Therapy for Hemophilia B Named ‘Orphan Drug’ by FDA
Sangamo BioSciences announced that its zinc finger nuclease (ZFN)-mediated genome editing product, SB-FIX, has received orphan drug designation from the…
Boy with Hemophilia A Undergoes Successful Stem Cell Transplant, Researchers Report
A number of clinical studies have reported that bone marrow-derived cells contribute to the production of clotting factor VIII (FVIII), the…
Brain Hemorrhage in Boy with Hemophilia Treated with Transfusions
Researchers in India recently reported the case of child with hemophilia and traumatic intracerebellar hemorrhage, who was successfully treated with transfusions of…
Porcine Recombinant Factor VIII Valid for Certain Hemophilia A, Review Suggests
In hemophilia A, the most significant therapeutic complication is the development of antibodies against factor VIII (FVIII) that inhibit its coagulant…
CSL Behring’s Therapy for Severe Hemophilia A Shows Promise in Clinical Study
CSL Behring’s rVIII-SingleChain, a novel recombinant Factor VIII (rFVIII) treatment candidate, recently demonstrated effectiveness in surgery and in the control of…
Ruptured Spleen in Newborn with Hemophilia A Treated Without Surgery
Ruptured spleens are rare in newborns, usually occurring secondary to an underlying coagulation disorder, such as hemophilia, or a splenic abnormality.
Researchers Question Health-Related Quality of Life for Youth, Young Men with Hemophilia
Researchers at several Canadian institutions investigated the tendencies of health-related quality of life (HRQoL) among teenagers and young adults with hemophilia…
Case Report: Acquired Hemophilia A with Bone Marrow Disorder
The association of hemophilia A (AHA) and myelofibrosis, a bone marrow disorder, is uncommon and rarely described but in a…
Economic Costs of Hemophilia, Large and Lifelong, Detailed in Report
In addition to its clinical challenges, hemophilia is characterized by a major economic burden that affects patients, care givers, the healthcare…