Rixubis safely and effectively prevents and manages bleeding in children and adults with hemophilia B, a real-world study from South Korea reports. The study, “Safety and effectiveness of Rixubis in patients with hemophilia B: a real-world, prospective, postmarketing surveillance study in South Korea,” was published in the journal Blood…

Complication rates for elective surgeries in people with inherited bleeding disorders like hemophilia are low in Australia, reflecting good safety in their performance despite guidelines not always being followed, a study reported. Use of a specialty hemophilia treatment center (HTC) for surgery, and use of factor replacement therapy were among guidelines sometimes…

The advancements in modern medicine have meant that people with hemophilia are living longer than ever, however, this brings its own set of problems for the medical profession. People living with the disease are just as likely to have other health issues when they get older as those without hemophilia,…

uniQure has treated the first patient in a Phase 2b dose-confirmation study of its investigational gene therapy, AMT-061, for people with severe and moderately severe hemophilia B. The trial is still recruiting participants. AMT-061 uses a viral vector, AAV5, to deliver the gene for a mutated clotting factor…

When you live with a bleeding disorder, you get used to explaining yourself. You learn to walk into an emergency room ready with a treatment letter and a mental script of your medical history. You learn to minimize pain, explain bruises, fight for treatment, and reassure medical professionals that, yes,…

Ease of use, fear of the unknown, and healthcare providers’ advice are all major factors that play a role in whether people with hemophilia want to switch to new treatment options, a small study suggests. The study, “Patient Perspectives on Novel Treatments in Haemophilia: A Qualitative Study,”…

I was pleasantly surprised to see a character with hemophilia depicted in a recent episode of “Call the Midwife,” a television series I adore. Usually, I’m disappointed with how hemophilia or von Willebrand disease is presented on TV, as it’s often inaccurate. This time, however, I felt the…

There are organizations all over the world that are dedicated to helping people with hemophilia and their loved ones. To make your search a little easier, we’ve listed some of the the more well-known ones below: National Hemophilia Foundation The NHF started in 1948, with the goals of discovering better treatments…

Therapeutic plasma exchange (TPE) was found to reduce bleeding and ease disease symptoms in six people with acquired hemophilia A (AHA), a case series reported. These findings support TPE — in which the liquid part of blood is replaced with substitute plasma — as an alternative treatment option in…