My husband, Jared, enjoys cooking. As I write this, a pot of gumbo simmers on the stove. Its strong aroma drifts throughout our open-layout house and toward my work desk. My stomach churns in excitement. It’s his first time making this dish, but as with nearly every recipe…
Search results for:
Preparing for change is never easy. For Caeleb, my youngest son, this season of his life is stressful yet exciting. After graduating from high school, he is marching on as a freshman at the University of New Mexico this fall. He’s excited about attending college, but has some…
Believe Limited, continuing a partnership with BioMarin Pharmaceutical and working with the Foundation for Art & Healing, announced plans to produce a documentary film on the everyday challenges and victories of living with a bleeding disorder. The digital content production company, again with the support of BioMarin, produced “…
The internet is overflowing with life hacks that can make tasks easier. From using a plastic knife to cleanly cut brownies to using pillowcases to clean ceiling fan blades, there are hundreds of tricks to help people solve problems. For example, I recently grabbed a roll of Press’n Seal…
News
Sigilon Therapeutics’ Afibromer SIG-003 for Long-term Treatement of Hemophilia B Advances in EU
Sigilon Therapeutics’s Afibromer SIG-003 candidate for the long-term treatment of patients with hemophilia B recently received an Advanced Therapy Medicinal Product (ATMP) designation in the European Union. The designation was granted by the Committee for Advanced Therapies of…
One of my favorite movies is “Galaxy Quest,” a comedy that parodies and pays homage to science fiction films and TV. In it, the cast members of a cult series much like “Star Trek” are drawn into an interstellar conflict by real aliens who think the series is…
The U.S. Food and Drug Administration (FDA) has granted orphan drug status (ODD) to Catalyst Biosciences’ highly potent recombinant human factor IX variant CB 2679d (also known as ISU304) to treat hemophilia B. Catalyst is evaluating CB 2679d’s potential for subcutaneous prophylactic treatment in people with hemophilia B. The regulatory decision…
Alaska, Antarctica, and Greenland have something in common: They’re a few of the places where glaciers are present. A glacier is a large, slow-moving mass of ice and snow that forms over an extended period in areas where more snow accumulates during the winter than melts during the summer. Many…
The biotech companies Swedish Orphan Biovitrum AB (Sobi) and Biogen have announced that the European Commission (EC) has approved their extended half-life therapy Alprolix (rFIXFc) for hemophilia B in all 28 European Union (EU) countries. In addition, the EC maintained the drug’s orphan designation. The World Federation of Hemophilia (WFH) estimated…
In our quest for security and certainty, it’s only natural to gravitate toward options that offer zero risk. Think about it: When you purchase insurance or opt for a product with a money-back guarantee, you’re essentially seeking assurance against any potential loss. This tendency to avoid risk at all…