The parents of most children with severe hemophilia A who took part in the XTEND-Kids clinical trial of Altuviiio (efanesoctocog alfa) reported in exit interviews that the once-weekly treatment led to notable improvements in mood for their sons, with some reporting a greater ability for their boys to…

“Huge Estate Sale: Hoarder House!” the advertisement said, offering 4,000 square feet of floor-to-ceiling treasures. The former occupant was a retired psychology professor named Bill who reportedly let no one into his home. When he died, his relatives entered his home for the first time. Forcing the front door open,…

I’m late getting my garden ready for the season. I considered giving in and leaving the weeds and remnants from last year’s harvest for another season, but seeing the butterflies and bees come to my space and picking fresh vegetables brings me too much happiness. So I enlisted my husband…

When my oldest son, Julian, was 5, our paths crossed in the medical world. My wife, Cazandra, was out of town, and my boy and I were holding down the fort at home. Julian had hemophilia with a low-titer inhibitor and thus needed to infuse factor VIII every day.

Sanofi has reduced the dosing of its investigational treatment fitusiran in clinical trials to lower the risk of blood clots in people with hemophilia, according to a joint statement representing patient organizations worldwide. In October 2020, the company placed a voluntary dosing hold on its full clinical…

Signs are appearing outside restrooms in the United Kingdom to advise members of the public that not all disabilities are visible. MORE: Learn more about hemophilia and what it really means to have the blood disorder. According to a report from the BBC, the signs are being posted to help those…

The U.S. Food and Drug Administration (FDA) has accepted a resubmitted biologics license application (BLA) from BioMarin Pharmaceutical requesting approval of the gene therapy Roctavian (valoctocogene roxaparvovec) to treat adults with severe hemophilia A. The FDA is now expected to decide by the end of March 2023 on whether…

Special education. Those two words strike fear into the hearts of many parents. “But my son doesn’t need special ed!” I know, because I was one of those moms. When my oldest son Julian, now 22, was in elementary school, the idea of a 504 plan — based…

Eptacog beta was safe and 100% effective at preventing bleeds during and after minor surgeries in hemophilia A patients with inhibitors, according to data from a Phase 3 trial. The treatment’s efficacy at managing bleeds dropped with major surgeries, with post-operative success seen in 66.7% of evaluated cases. Overall, these…

I’ve been struggling with hip bleeds lately. I’m in the middle of recovering from a bleed on my right hip, which may have started because I put too much pressure on it too soon. I’m frustrated that I’ve been bedridden so often these past few months. It’s hard…