For Bleeding Disorders Awareness Month, stressing safe treatment use
In observance of Bleeding Disorders Awareness Month, the integrated infusion therapy provider BioTek reMEDys is calling attention to…
Articles by Mary Chapman
Monthslong shortage forecast for Rebinyn 3,000 IU for hemophilia B
Unexpectedly high demand for the 3,000 international units (IU) vial size of Rebinyn (nonacog beta pegol) has resulted in…
Hemgenix given to 1st patient in Florida at Tampa General Hospital
Tampa General Hospital’s cancer institute is the first healthcare center in Florida, and the third in the U.S., to successfully…
Partnership expands access in EU to Roctavian companion diagnostic test
A partnership between ARUP Laboratories and Medicover will improve access to AAV5 DetectCDx, the former’s companion diagnostic…
German health insurance fund to reimburse Roctavian for hem A
Eligible patients with severe hemophilia A in Germany should now have improved access to Roctavian (valoctocogene roxaparvovec-rvox) — a…
FDA awards support Sernova’s work into Cell Pouch for hemophilia A
The U.S. Food and Drug Administration (FDA) has given orphan drug and rare pediatric disease designations to Sernova’s…
Genevant, Novo Nordisk partner on gene-editing treatment for hem A
Genevant Sciences is teaming up with Novo Nordisk to develop a gene-editing treatment for hemophilia A that…
Prix Galien USA award goes to CSL and uniQure for Hemgenix
Hemgenix (etranacogene dezaparvovec), the first and only gene therapy approved for adults with hemophilia B, has won this…
Hope Conference set to educate Nov. 2-4 in person and online
This year’s Hope Conference, a national educational event presented by Hope Charities for the bleeding disorders community, is set…
Pathway to Cures philanthropy fund grows with first new donor
Two longtime bleeding disorders advocates, who are the parents of a son with hemophilia B, have made a founding…