Two potential gene therapies — AMT-060 and AMT-061 (etranacogene dezaparvovec) — lead to safe and long-term increases in factor IX (FIX) activity, as well as fewer bleeds among patients with hemophilia B, according to the therapies’ maker, uniQure. The company announced in a press release that…

Want to be happier and more content in life? Embrace change, a study published in The Review of Economic Studies notes. I did a double take when I first read about the study at cnbc.com. Oftentimes, change and contentment are presented as completely opposing ideas. The stereotypically “content”…

A web-based software to help personalize dosing regimens for hemophilia A patients being treated with Adynovate is now available in the U.S., according to Takeda. The software, called myPKFiT, previously was available only for individuals being treated with Advate. For Adynovate, it is to be used by…

People are suffering. The country is divided. States are imposing limits on items that may be purchased, and businesses are closed. If there were ever a year to skip Thanksgiving, this would be it. At least, that is what some people think, but I am not one of them. It…

The first participant was dosed with the investigational therapy marstacimab in a Phase 3 clinical trial — still recruiting eligible patients across the globe — in adolescents and adults with severe hemophilia A or B. Pfizer‘s marstacimab (PF‐06741086) is a human antibody that blocks a…

The healthcare insurance company BCS Financial has partnered with the National Hemophilia Foundation (NHF) to improve care quality and cost for people with hemophilia. BCS Financial provides services primarily for Blue Cross and Blue…

Let’s face it. This year contains one struggle after another. We continue to ask the same questions: “How do we beat this virus? Will I continue to be insured during layoffs? How will I afford quality care for my loved one in the middle of political, medical, and economic turmoil?”…

When my husband, Jared, and I were dating, many of our friends thought we had the perfect relationship. We were snuggly best buddies, intimate and passionate lovers, and mentors to each other. It was a bond I could only describe as spiritual and otherworldly. I had never met anyone who…

Due to the identification of new adverse events, Sanofi Genzyme has placed a dosing hold on its full clinical development program for fitusiran, an investigational treatment for hemophilia. The decision was announced in a joint statement from the World Federation of Hemophilia, the European…

We all live according to life lessons. Not every way by which we govern our lives proves useful or affirming, but the lessons still unknowingly exist. My goal is to identify the negative patterns that I relate to the world and change them so that my actions match my desired…