A committee of the European Medicines Agency (EMA) has issued a positive opinion recommending the one-time gene therapy etranacogene dezaparvovec be granted conditional marketing authorization to treat appropriate adults with hemophilia B. The recommendation from the EMA’s Committee for Medicinal Products for Human Use (CHMP) will now be…

As we prepare to celebrate Christmas, I can’t help but remember a particular year in the MacDonald household. In 2013, my youngest son, Caeleb, couldn’t catch a break from hemophilia. Constant spontaneous bleeding episodes into his right knee and ankle kept my boy in the hospital more often…

I am not a fan of roller coasters. Dropping straight down in a car on a wooden track makes me feel like my heart has left my body. Why would anyone want to feel that way? However, I have one exception: the Rock ‘n’ Roller Coaster Starring Aerosmith…

With 2022 soon coming to a close, I can’t help but wonder what kind of year is going to take its place. So much has happened in the past three years, since my daughter, Cittie, was born. Yet when I look at my pictures then, I don’t feel like I’m…

Last week, I set out in my car to donate some household items to Goodwill. I’ve been there probably a dozen times, but this time I drove past the Goodwill building twice. Why? Because my community is missing signs. All kinds of signs. Street signs, building signs, and even stop…

I recently bought an unexpectedly large number of indoor plants. After previously having just one living room plant and a dying cactus, I suddenly had an epiphany about redecorating with multiple houseplants. I managed to create a relaxing sanctuary, and now every day feels like a tiny vacation! Since my…

AvevoRx is entering the bleeding disorders market with a program aimed at addressing the dearth of accessible, personalized specialty infusion and pharmacy services for people with hemophilia and related conditions. The North Carolina-based company, founded last year, provides specialty infusion pharmacy services in several states to at-home patients who have…

I tell my sons that I love them every day and at the end of every conversation. I can count on one hand the number of days I haven’t spoken to them. However, sometimes I fear my words fall on deaf ears, as my pronouncement of devotion may sound repetitive…

I’ve been reading quite a bit of philosophy in my free time lately. Right now I’m reading the works of Seneca, a first-century Stoic philosopher. I’ve always been interested in Stoic philosophy and its teachings. As a field of study, Stoicism is concerned mainly with how humans can attain…

I do not give up. It’s in my DNA to find answers to questions, even if it takes a long time. I hope my sons, who both have hemophilia, inherit this characteristic of seeking out answers. I pray they have the strength to never accept defeat. I tell them…