AvevoRx is entering the bleeding disorders market with a program aimed at addressing the dearth of accessible, personalized specialty infusion and pharmacy services for people with hemophilia and related conditions. The North Carolina-based company, founded last year, provides specialty infusion pharmacy services in several states to at-home patients who have…

I tell my sons that I love them every day and at the end of every conversation. I can count on one hand the number of days I haven’t spoken to them. However, sometimes I fear my words fall on deaf ears, as my pronouncement of devotion may sound repetitive…

BioMatrix Specialty Pharmacy has announced the six recipients of this year’s Memorial Scholarship Program, with each receiving $1,000 to support their higher education. The program, a partnership with the Hemophilia Federation of America (HFA), honors the memory of people who uniquely impacted the bleeding disorders community…

I’ve been reading quite a bit of philosophy in my free time lately. Right now I’m reading the works of Seneca, a first-century Stoic philosopher. I’ve always been interested in Stoic philosophy and its teachings. As a field of study, Stoicism is concerned mainly with how humans can attain…

Changes in the cellular microenvironment could influence immune responses against factor VIII (FVIII) replacement therapy in people with hemophilia A, a new study suggests. Data from the cell culture study showed that FVIII proteins that cause an immune reaction differ depending on which other molecules are present in…

I do not give up. It’s in my DNA to find answers to questions, even if it takes a long time. I hope my sons, who both have hemophilia, inherit this characteristic of seeking out answers. I pray they have the strength to never accept defeat. I tell them…

I spend a lot of time in the kitchen during the holiday season. I enjoy creating my favorite dishes and finding new and exciting recipes. Many people follow recipes strictly, but I find joy in realizing they’re more of a guide than an exact science. Using a guide to cook…

A review is continuing into a resubmitted application for approval of Roctavian (valoctocogene roxaparvovec), a gene therapy for adults with severe hemophilia A, with a planned advisory committee meeting having been canceled. The U.S. Food and Drug Administration (FDA) had requested, but now no longer intends, to meet with…

Today, as we take time to celebrate the gift of one another, I can’t help but think about the many trials my 16-year-old son, Caeleb, faced this year as a result of hemophilia. As a child, Caeleb struggled with frequent breakthrough bleeds, which have left him with excruciating…

The first gene therapy for adults with hemophilia B — branded as Hemgenix (etranacogene dezaparvovec) — has been approved by the U.S. Food and Drug Administration (FDA). Meant to be a one-time treatment, Hemgenix is expected to keep bleeding in check in the long term, while also allowing patients…